Category:Orphan drugs
From WikiMD.com Medical Encyclopedia
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
- FDA List of Orphan Designations and Approvals [dead link]
- European Commission Register of designated Orphan Medicinal Products
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 314 total.
(previous page) (next page)A
- Acalabrutinib
- Acetohydroxamic acid
- Actemra
- Adagrasib
- Alglucosidase alfa
- Alpha-1-Proteinase Inhibitor (Human)
- Altretamine
- Alvocidib
- Amifampridine
- Dalfampridine
- Amitriptyline
- Anacaulase
- Anagrelide
- Ansuvimab-zykl
- Artesunate
- Asciminib
- Asfotase alfa
- Atoltivimab, maftivimab, and odesivimab-ebgn
- Atoltivimab/maftivimab/odesivimab
- Avacopan
- Avalglucosidase alfa
- Avapritinib
- Avatrombopag
- Avelumab
- Axicabtagene ciloleucel
- Vidaza
B
- Baloxavir marboxil
- Belantamab mafodotin
- Belantamab mafodotin-blmf
- Belumosudil
- Belzutifan
- Benralizumab
- Berotralstat
- Bevacizumab
- Binimetinib
- Bortezomib
- Bosentan
- Brentuximab vedotin
- Brexucabtagene autoleucel
- Brigatinib
- Briumvi
- Budesonide
- Budesonide Oral Inhalation
- Buprenorphine + Naloxone
- Buprenorphine/naloxone
- Burosumab
- Busulfan
C
- Cabometyx
- Cabozantinib
- Caffeine citrate
- Calaspargase pegol
- Xywav
- Caplacizumab
- Caplacizumab-yhdp
- Capmatinib
- Carboprost
- Carglumic acid
- Carmustine
- Cerliponase alfa
- Ciltacabtagene autoleucel
- Cipaglucosidase alfa
- Cladribine
- Cobimetinib
- Colchicine
- Cometriq
- Conestat alfa
- Copper (64Cu) oxodotreotide
- Crizanlizumab
- Crizanlizumab-tmca
- Cystaran
- Cysteamine bitartrate
D
E
G
I
K
L
- L-asparaginase
- Lanadelumab-flyo
- Laronidase
- Larotrectinib
- Lecanemab
- Lenacapavir
- Leniolisib
- Lenvatinib
- Letermovir
- Lisocabtagene maraleucel
- Lomitapide mesylate
- Lonapegsomatropin
- Loncastuximab tesirine-lpyl
- Lorlatinib
- Losartan
- Lovotibeglogene autotemcel
- Lumacaftor and ivacaftor
- Lurbinectedin
- Luspatercept–aamt
- Lusutrombopag
- Lutetium Lu 177 dotatate
- Lutetium Lu 177-dotatate
M
- Maralixibat
- Margetuximab
- Maribavir
- Mavacamten
- Mavenclad
- Mechlorethamine
- Melphalan flufenamide
- Mepolizumab
- Methotrexate
- Metreleptin
- Migalastat
- Migalastat hydrochloride
- Miglustat
- Milrinone
- Mitapivat
- Mitomycin
- Mitomycin Pyelocalyceal
- Mobocertinib
- Mogamulizumab-kpkc
- Mosunetuzumab
- Moxetumomab pasudotox-tdfk
- Moxidectin
- Mycapssa
