Category:Orphan drugs
From WikiMD's Food, Medicine & Wellnesspedia
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 331 total.
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- Acalabrutinib
- Acetohydroxamic acid
- Actemra
- Adagrasib
- Afamelanotide
- Alglucosidase alfa
- Alpha 1 Antitrypsin deficiency
- Alpha-1-Proteinase Inhibitor (Human)
- Altretamine
- Alvocidib
- Amifampridine
- Dalfampridine
- Amitriptyline
- Anacaulase
- Anagrelide
- Anisina
- Ansuvimab-zykl
- Anti-CD37 antibody-drug conjugate IMGN529
- Anti-transforming growth factor beta (TGF-ß) trap fusion protein
- Artesunate
- Asciminib
- Asfotase alfa
- Asparaginase erwinia chrysanthemi (recombinant)-rywn
- Atoltivimab, maftivimab, and odesivimab-ebgn
- Atoltivimab/maftivimab/odesivimab
- Avacopan
- Avalglucosidase alfa
- Avalglucosidase alfa-ngpt
- Avapritinib
- Avatrombopag
- Avelumab
- Axicabtagene ciloleucel
- Vidaza
B
- Baloxavir marboxil
- Belantamab mafodotin
- Belantamab mafodotin-blmf
- Belumosudil
- Belzutifan
- Benralizumab
- Berotralstat
- Bevacizumab
- Binimetinib
- Bortezomib
- Bosentan
- Brentuximab vedotin
- Brexucabtagene autoleucel
- Brigatinib
- Briumvi
- Budesonide
- Budesonide Oral Inhalation
- Buprenorphine + Naloxone
- Buprenorphine/naloxone
- Burosumab
- Busulfan
C
- Cabometyx
- Cabozantinib
- Caffeine citrate
- Calaspargase pegol
- Xywav
- Caplacizumab
- Caplacizumab-yhdp
- Capmatinib
- Carboprost
- Carglumic acid
- Carmustine
- Carmustine implant
- Casimersen
- Cerliponase alfa
- Cholic acid
- Ciltacabtagene autoleucel
- Cipaglucosidase alfa
- Cladribine
- Cobimetinib
- Colchicine
- Cometriq
- Conestat alfa
- Copper (64Cu) oxodotreotide
- Crizanlizumab
- Crizanlizumab-tmca
- Cystaran
- Cysteamine bitartrate
D
E
F
G
I
K
L
- L-asparaginase
- Lanadelumab-flyo
- Laronidase
- Larotrectinib
- Lecanemab
- Lenacapavir
- Leniolisib
- Lenvatinib
- Letermovir
- Lisocabtagene maraleucel
- Lomitapide mesylate
- Lonafarnib
- Lonapegsomatropin
- Loncastuximab tesirine-lpyl
- Lorlatinib
- Losartan
- Lovotibeglogene autotemcel
- Lumacaftor and ivacaftor
- Lumasiran
- Lurbinectedin
- Luspatercept–aamt
- Lusutrombopag
- Lutetium Lu 177 dotatate
- Lutetium Lu 177-dotatate
M
- Maralixibat
- Margetuximab
- Maribavir
- Mavacamten
- Mavenclad
- Mechlorethamine
- Melphalan flufenamide
- Mepolizumab
- Methotrexate
- Metreleptin
- Migalastat
- Migalastat hydrochloride
- Miglustat
- Milrinone
- Mitapivat
- Mitomycin
- Mitomycin Pyelocalyceal
- Mobocertinib
- Mogamulizumab-kpkc
- Mosunetuzumab
- Moxetumomab pasudotox-tdfk
- Moxidectin
- Mycapssa
